Gene Therapy

Welcome!

We are delighted that you have chosen the Therapeutic Modalities module to start or enhance your current educational journey in immuno-safety science. This lecture is one in a series of five providing detailed information on current and/or emerging therapeutics that interact with the immune system. Please review the learning objectives below for more information on what you will learn in this lecture.
 
If you are new to HESI and would like to learn more about our organization, please take a moment to visit our website at  https://hesiglobal.org/.

Target Audience

This course is intended for the science professional or graduate student looking to learn the fundamental science and key consideration that are examined in immune safety assessment. Advanced topics and coursed that take a deeper dive into specific scientific areas will be offered and are recommended for the more experienced scientist who has a firm grasp of the information highlighted in the introduction module.

Learning Objectives

 
The learner will:
 
  • Become familiar with the field of gene therapy.
  • Gain understanding of the use recombinant AAV vectors in gene therapy.
  • Introduction to genome editing and gene regulation technologies.
  • Understand the considerations for designing nonclinical programs.
  • Nonclinical safety evaluation strategies for gene therapy investigational products.

Additional Information

AttachmentSize
PDF icon Gene Therapy slide deck - Meyer6.03 MB
Course summary
Available credit: 
  • 0.50 Participation
Course opens: 
03/22/2022
Course expires: 
03/31/2027
Cost:
$25.00
Part of: 
Therapeutic Modalities
Rating: 
0

Lectures in this module

 
CAR Therapy
 
Safety Considerations for Oligonucleotides
 
CD3-binding (T cell engaging) immune stimulating antibody-based therapies
 
Gene Therapy
 
Nonclinical Development of Biologics
Kathleen Meyer, MPH, PhD, DABT
Sangamo Therapeutics

Available Credit

  • 0.50 Participation

Price

Cost:
$25.00
Please login or register to take this course.

Required Hardware/software

This platform, Ethos CE, works with most modern web browsers (e.g., Chrome, Internet Explorer, MS Edge, Safari). Contact itc@hesiglobal.org if you are having any difficulties with this platform.