
Gene Therapies
Learning Objectives
- Become familiar with the field of gene therapy
- Gain understanding of the use recombinant AAV vectors in gene therapy
- Introduction to genome editing and gene regulation technologies
- Understand the considerations for designing nonclinical programs
- Nonclinical safety evaluation strategies for gene therapy investigational products
Kathleen Meyer, PhD
Vice President, Nonclinical Development
Sangamo Therapeutics Incorporated